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Baby is healed with first personalized gene-editing treatment

(www.nytimes.com)
1163 points jbredeche | 2 comments | 15 May 25 18:06 UTC | HN request time: 0.428s | source
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MrZander ◴[15 May 25 19:30 UTC] No.43998447[source]▶
> To accomplish that feat, the treatment is wrapped in fatty lipid molecules to protect it from degradation in the blood on its way to the liver, where the edit will be made. Inside the lipids are instructions that command the cells to produce an enzyme that edits the gene. They also carry a molecular GPS — CRISPR — which was altered to crawl along a person’s DNA until it finds the exact DNA letter that needs to be changed.

That is one of the most incredible things I have ever read.

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1. esalman ◴[16 May 25 06:13 UTC] No.44002289[source]▶
Thanks to DOGE you might read less and less about this kind of things.
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2. shafyy ◴[16 May 25 08:50 UTC] No.44003155[source]▶
Unfortunately, this is true. From the article:

> The implications of the treatment go far beyond treating KJ, said Dr. Peter Marks, who was the Food and Drug Administration official overseeing gene-therapy regulation until he recently resigned over disagreements with Robert F. Kennedy Jr., the secretary of health and human services.